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Sangamo Fabry LTFU Study Protocol ST-920-LT01

UCI Specialty Area: Genetics
Principal Investigator: Madeleine Pahl
Official Title: Long-Term Follow-up of Fabry Disease Subjects who have Undergone IV Infusion with ST-920, an rAAV2/6 Human Alpha Galactosidase A Gene Therapy
A Study On:
Fabry Disease

Study Description

This is a multi-center, long-term follow-up (LTFU) study of subjects who received ST-920 in a

separate parent trial. At the final visit of parent trial, the Investigator or designated study

personnel will review the informed consent form (ICF) for this LTFU study with the study

subject. After informed consent is obtained, subjects will be followed for up to 5 years from

infusion.

Eligibility

  • Subjects who received ST-920 therapy in a separate parent trial.
  • Subjects who have consented to participate in this LTFU study.

This study does not have any exclusion criteria

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Privacy Policy

University of California, Irvine - Study Information Sheet

UCI Center for Clinical Research Potential Participant Database

Lead Researcher
Maheswari Senthil, MD
UCI Center for Clinical Research

In the instance of parental permission, “You” refers to “Your child.”

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  • Future Research Use
    Researchers will use your information to conduct this study. Once the study is done using your information, we may share them with other researchers so they can use them for other studies in the future. We will not share your name or any other private identifiable information that would let the researchers know who you are. We will not ask you for additional permission to share this de-identified information
  • Data Retention - In accordance with UC Office of the President policy, information will be retained for 10 years after the end of the calendar year in which the research is completed.
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